The workshop—co-chaired by Glenn Pierce, MD, PhD, Vice President, Medical, WFH, and David Lillicrap, MD—has been held every few years since 1966. The high-level scientific meeting brings together experts from various fields, including immunologists, clinicians, researchers, regulators, and patients to discuss the latest advancements and challenges in the field of gene therapy for hemophilia.
During the 2½-day event, presentations covered a wide range of topics, from laboratory science to clinical trials. The workshop provided an opportunity for experts in the field to share their latest findings, collaborate on innovative approaches, and discuss challenges facing gene therapy for hemophilia. Overall, the workshop emphasized the need for continued research, development, and innovation to advance treatment options for those with hemophilia.
Click here or click on the player below to watch a video where Pierce summarizes and highlights some of the key themes that emerged from the meeting, including the latest findings on liver health, immunosuppression, and insertional mutagenesis.