{"id":129116,"date":"2024-11-19T09:00:20","date_gmt":"2024-11-19T14:00:20","guid":{"rendered":"https:\/\/wfh.org\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/"},"modified":"2024-11-27T09:49:42","modified_gmt":"2024-11-27T14:49:42","slug":"le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal","status":"publish","type":"post","link":"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/","title":{"rendered":"Le tout premier atelier men\u00e9 par la FMH sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique s\u2019est tenu \u00e0 Montr\u00e9al"},"content":{"rendered":"\t\t<div data-elementor-type=\"wp-post\" data-elementor-id=\"129116\" class=\"elementor elementor-129116 elementor-129094\" data-elementor-post-type=\"post\">\n\t\t\t\t\t\t<section class=\"elementor-section elementor-top-section elementor-element elementor-element-4a918ea elementor-section-boxed elementor-section-height-default elementor-section-height-default\" data-id=\"4a918ea\" data-element_type=\"section\" data-e-type=\"section\">\n\t\t\t\t\t\t<div class=\"elementor-container elementor-column-gap-default\">\n\t\t\t\t\t<div class=\"elementor-column elementor-col-100 elementor-top-column elementor-element elementor-element-563305e\" data-id=\"563305e\" data-element_type=\"column\" data-e-type=\"column\">\n\t\t\t<div class=\"elementor-widget-wrap elementor-element-populated\">\n\t\t\t\t\t\t<div class=\"elementor-element elementor-element-7180ab0 elementor-widget elementor-widget-text-editor\" data-id=\"7180ab0\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t<div class=\"elementor-widget-container\">\n\t\t\t\t\t\t\t\t\t<p>L\u2019atelier sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique se tient depuis 1996 \u00e0 quelques ann\u00e9es d\u2019intervalle, et a r\u00e9cemment \u00e9t\u00e9 anim\u00e9 par la National Bleeding Disorders Foundation (NBDF). En s\u2019appuyant sur tout cet historique, la FMH a organis\u00e9 la 18<sup>e<\/sup> \u00e9dition, poursuivant une longue tradition d\u2019am\u00e9lioration des soins pour les personnes atteintes d\u2019h\u00e9mophilie gr\u00e2ce \u00e0 la recherche de pointe.<\/p>\n<p>Le premier jour de l\u2019atelier s\u2019est concentr\u00e9 sur les probl\u00e8mes d\u2019immunologie et les toxicit\u00e9s associ\u00e9es au transfert de g\u00e8nes, sur les anticorps monoclonaux et bisp\u00e9cifiques pour l\u2019h\u00e9mophilie et les autres troubles de la coagulation, ainsi que sur la th\u00e9rapie g\u00e9nique non virale et l\u2019\u00e9dition g\u00e9nomique.<\/p>\n<p>Les pr\u00e9sentations de la deuxi\u00e8me journ\u00e9e ont abord\u00e9 le besoin d\u2019am\u00e9lioration des transg\u00e8nes du FVIII et de leurs alternatives, les autres syst\u00e8mes de vecteur et les essais cliniques innovants, et les derni\u00e8res avanc\u00e9es en mati\u00e8re de vecteurs AAV. Un panel de patient\u00b7es a \u00e9galement discut\u00e9 de l\u2019\u00e9tat de la science.<\/p>\n<p>Le 18<sup>e<\/sup> atelier sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique a \u00e9t\u00e9 une opportunit\u00e9 unique pour les participant\u00b7es de se rassembler, soulignant ainsi l\u2019engagement de la communaut\u00e9 en faveur de l\u2019avanc\u00e9e des nouvelles technologies et de l\u2019assurance que les traitements innovants puissent b\u00e9n\u00e9ficier \u00e0 l\u2019ensemble des patient\u00b7es.<\/p>\n<p><em>Le 18<sup>e<\/sup> atelier sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique a b\u00e9n\u00e9fici\u00e9 du soutien de\u00a0:<\/em><br \/>\n<em>Partenaires visionnaires\u00a0: CSL Behring et Spark Therapeutics<\/em><br \/>\n<em>Partenaire leader\u00a0: Pfizer<\/em><br \/>\n<em>Partenaire collaborateur : Biomarin<\/em><br \/>\n<em>Nos remerciements vont \u00e9galement \u00e0 HC Bioscience, Hemab, Metagenomi, NBDF, STAR therapeutics<\/em><\/p>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t<\/section>\n\t\t\t\t<\/div>\n\t\t","protected":false},"excerpt":{"rendered":"<p>La 18e \u00e9dition de l\u2019Atelier de la FMH sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique, dirig\u00e9 par la FMH pour la premi\u00e8re fois, a eu lieu en pr\u00e9sentiel les 7 et 8 novembre 2024. Cette r\u00e9union scientifique restreinte de haut niveau a rassembl\u00e9 pr\u00e8s de 70 expert\u00b7es de divers domaines \u2013 immunologues, clinicien\u00b7nes, chercheurs et chercheuses, patient\u00b7es \u2013 pour explorer de nouveaux territoires dans le traitement de l\u2019h\u00e9mophilie. Cet atelier a \u00e9t\u00e9 l\u2019occasion pour les expert\u00b7es de partager leurs derni\u00e8res d\u00e9couvertes, de collaborer sur des approches innovantes et de discuter des difficult\u00e9s li\u00e9es aux technologies nouvelles pour l\u2019h\u00e9mophilie, ce qui inclut entre autres la th\u00e9rapie g\u00e9nique. <\/p>\n","protected":false},"author":13,"featured_media":129103,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"inline_featured_image":false,"footnotes":""},"categories":[114,334],"tags":[],"search-category":[85],"class_list":["post-129116","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-education-fr","category-featured-1-fr","search-category-article"],"yoast_head":"<!-- This site is optimized with the Yoast SEO Premium plugin v27.2 (Yoast SEO v27.2) - https:\/\/yoast.com\/product\/yoast-seo-premium-wordpress\/ -->\n<title>Le tout premier atelier men\u00e9 par la FMH sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique s\u2019est tenu \u00e0 Montr\u00e9al | FMH - F\u00e9d\u00e9ration mondiale de l\u2019h\u00e9mophilie<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/\" \/>\n<meta property=\"og:locale\" content=\"fr_FR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Le tout premier atelier men\u00e9 par la FMH sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique s\u2019est tenu \u00e0 Montr\u00e9al\" \/>\n<meta property=\"og:description\" content=\"La 18e \u00e9dition de l\u2019Atelier de la FMH sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique, dirig\u00e9 par la FMH pour la premi\u00e8re fois, a eu lieu en pr\u00e9sentiel les 7 et 8 novembre 2024. Cette r\u00e9union scientifique restreinte de haut niveau a rassembl\u00e9 pr\u00e8s de 70 expert\u00b7es de divers domaines \u2013 immunologues, clinicien\u00b7nes, chercheurs et chercheuses, patient\u00b7es \u2013 pour explorer de nouveaux territoires dans le traitement de l\u2019h\u00e9mophilie. Cet atelier a \u00e9t\u00e9 l\u2019occasion pour les expert\u00b7es de partager leurs derni\u00e8res d\u00e9couvertes, de collaborer sur des approches innovantes et de discuter des difficult\u00e9s li\u00e9es aux technologies nouvelles pour l\u2019h\u00e9mophilie, ce qui inclut entre autres la th\u00e9rapie g\u00e9nique.\" \/>\n<meta property=\"og:url\" content=\"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/\" \/>\n<meta property=\"og:site_name\" content=\"FMH - F\u00e9d\u00e9ration mondiale de l\u2019h\u00e9mophilie\" \/>\n<meta property=\"article:publisher\" content=\"https:\/\/www.facebook.com\/wfhemophilia\/\" \/>\n<meta property=\"article:published_time\" content=\"2024-11-19T14:00:20+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2024-11-27T14:49:42+00:00\" \/>\n<meta property=\"og:image\" content=\"https:\/\/wfh.org\/wp-content\/uploads\/2024\/11\/New-Technology-and-Gene-Therapy-Workshop-wrapup-header.jpg\" \/>\n\t<meta property=\"og:image:width\" content=\"1200\" \/>\n\t<meta property=\"og:image:height\" content=\"627\" \/>\n\t<meta property=\"og:image:type\" content=\"image\/jpeg\" \/>\n<meta name=\"author\" content=\"Mitch Semienchuk\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:label1\" content=\"\u00c9crit par\" \/>\n\t<meta name=\"twitter:data1\" content=\"Mitch Semienchuk\" \/>\n\t<meta name=\"twitter:label2\" content=\"Dur\u00e9e de lecture estim\u00e9e\" \/>\n\t<meta name=\"twitter:data2\" content=\"1 minute\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\/\/schema.org\",\"@graph\":[{\"@type\":\"Article\",\"@id\":\"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/#article\",\"isPartOf\":{\"@id\":\"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/\"},\"author\":{\"name\":\"Mitch Semienchuk\",\"@id\":\"https:\/\/wfh.org\/fr\/#\/schema\/person\/4aea5b13c1966452a640eef39423925b\"},\"headline\":\"Le tout premier atelier men\u00e9 par la FMH sur les nouvelles technologies et la th\u00e9rapie g\u00e9nique s\u2019est tenu \u00e0 Montr\u00e9al\",\"datePublished\":\"2024-11-19T14:00:20+00:00\",\"dateModified\":\"2024-11-27T14:49:42+00:00\",\"mainEntityOfPage\":{\"@id\":\"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/\"},\"wordCount\":315,\"publisher\":{\"@id\":\"https:\/\/wfh.org\/fr\/#organization\"},\"image\":{\"@id\":\"https:\/\/wfh.org\/fr\/article\/le-tout-premier-atelier-mene-par-la-fmh-sur-les-nouvelles-technologies-et-la-therapie-genique-sest-tenu-a-montreal\/#primaryimage\"},\"thumbnailUrl\":\"https:\/\/wfh.org\/wp-content\/uploads\/2024\/11\/New-Technology-and-Gene-Therapy-Workshop-wrapup-header.jpg\",\"articleSection\":[\"\u00c9ducation\",\"Featured 1 - 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